University of Pennsylvania

“Baby KJ received a custom gene-editing therapy for a rare ammonia-processing disorder and is now a toddler who walks and talks. The treatment cost about $1.5M to make and deliver.”

“TiPToP achieves comparable or better success rates across diverse tasks, and we find that the two systems fail in complementary ways.”

“Dinesh Jayaraman advised the evaluations at the University of Pennsylvania and provided lab resources.”